Table of Contents
Table of Contents
Table of Contents 2
List of Tables 5
List of Figures 6
Introduction 7
Inherited Metabolic Disorders 7
Report Guidance 7
Clinical Trials by Region 8
Clinical Trials by Country 9
Top Countries Contributing to Clinical Trials in Asia-Pacific 11
Top Five Countries Contributing to Clinical Trials in Europe 12
Top Countries Contributing to Clinical Trials in North America 13
Top Countries Contributing to Clinical Trials in Middle East and Africa 14
Clinical Trials by BRIC Nations 15
Clinical Trials by G7 Nations 16
Clinical Trials in G7 Nations by Trial Status 17
Clinical Trials by E7 Nations 18
Clinical Trials in E7 Nations by Trial Status 19
Clinical Trials by Phase 20
In Progress Trials by Phase 21
Clinical Trials by Trial Status 22
Unaccomplished Trials of Inherited Metabolic Disorders 23
Subjects Recruited Over a Period of Time 25
Prominent Sponsors 26
Top Companies Participating in Inherited Metabolic Disorders Therapeutics Clinical Trials 28
Prominent Drug Comparison 30
Clinical Trial Profiles 31
Clinical Trial Overview of Top Companies 31
Genzyme Corporation 31
Clinical Trial Overview of Genzyme Corporation 31
Sanofi 32
Clinical Trial Overview of Sanofi 32
Synageva BioPharma Corp. 33
Clinical Trial Overview of Synageva BioPharma Corp. 33
Shire Plc 34
Clinical Trial Overview of Shire Plc 34
Raptor Pharmaceuticals Corp. 35
Clinical Trial Overview of Raptor Pharmaceuticals Corp. 35
Amsterdam Molecular Therapeutics (AMT) Holding N.V. 36
Clinical Trial Overview of Amsterdam Molecular Therapeutics (AMT) Holding N.V. 36
Actelion Pharmaceuticals Ltd 37
Clinical Trial Overview of Actelion Pharmaceuticals Ltd 37
U.S. Biotest Inc. 38
Clinical Trial Overview of U.S. Biotest Inc. 38
Edison Pharmaceuticals, Inc. 39
Clinical Trial Overview of Edison Pharmaceuticals, Inc. 39
Promethera Biosciences S.A. 40
Clinical Trial Overview of Promethera Biosciences S.A. 40
ReceptoPharm, Inc. 41
Clinical Trial Overview of ReceptoPharm, Inc. 41
Repligen Corporation 42
Clinical Trial Overview of Repligen Corporation 42
Zambon Company S.p.A. 43
Clinical Trial Overview of Zambon Company S.p.A. 43
Actelion Ltd 44
Clinical Trial Overview of Actelion Ltd 44
Clinical Trial Overview of Top Universities / Institutes / Hospitals 45
Oregon Health and Science University 45
Clinical Trial Overview of Oregon Health and Science University 45
Masonic Cancer Center 46
Clinical Trial Overview of Masonic Cancer Center 46
Baylor College of Medicine 47
Clinical Trial Overview of Baylor College of Medicine 47
Centre Hospitalier Universitaire de Nice 48
Clinical Trial Overview of Centre Hospitalier Universitaire de Nice 48
University of California, San Diego 49
Clinical Trial Overview of University of California, San Diego 49
Children's Research Institute 50
Clinical Trial Overview of Children's Research Institute 50
The Children's Hospital Los Angeles 51
Clinical Trial Overview of The Children's Hospital Los Angeles 51
New York Medical College 52
Clinical Trial Overview of New York Medical College 52
Semmelweis University 53
Clinical Trial Overview of Semmelweis University 53
Peking University 54
Clinical Trial Overview of Peking University 54
Rennes University Hospital 55
Clinical Trial Overview of Rennes University Hospital 55
University of Leipzig 56
Clinical Trial Overview of University of Leipzig 56
Children's Hospital Boston 57
Clinical Trial Overview of Children's Hospital Boston 57
University Hospital Hamburg-Eppendorf 58
Clinical Trial Overview of University Hospital Hamburg-Eppendorf 58
Far Eastern Memorial Hospital 59
Clinical Trial Overview of Far Eastern Memorial Hospital 59
University of Sao Paulo 60
Clinical Trial Overview of University of Sao Paulo 60
Northwestern University 61
Clinical Trial Overview of Northwestern University 61
McGill University Health Center 62
Clinical Trial Overview of McGill University Health Center 62
Sheba Medical Center 63
Clinical Trial Overview of Sheba Medical Center 63
University of Louisville 64
Clinical Trial Overview of University of Louisville 64
Five Key Clinical Profiles 65
Appendix 103
Abbreviations 103
Definitions 103
Research Methodology 104
Secondary Research 104
About GlobalData 105
Contact Us 105
Disclaimer 105
Source 106
List of Tables
List of Tables
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials by Zone, 2012* 8
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials by Top Countries, 2012* 9
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials In Progress by Top Countries, 2012* 10
Inherited Metabolic Disorders Therapeutics Clinical Trials, Asia-Pacific, Top Countries, 2012* 11
Inherited Metabolic Disorders Therapeutics Clinical Trials, Europe, Top Five Countries, 2012* 12
Inherited Metabolic Disorders Therapeutics Clinical Trials, North America, Top Countries, 2012* 13
Inherited Metabolic Disorders Therapeutics Clinical Trials, Middle East and Africa, Top Countries, 2012* 14
Inherited Metabolic Disorders Therapeutics Clinical Trials, BRIC Countries, 2012* 15
Inherited Metabolic Disorders Therapeutics Clinical Trials, G7 Countries, 2012* 16
Inherited Metabolic Disorders Therapeutics Market, G7 Countries, Clinical Trials by Trial Status, 2012* 17
Inherited Metabolic Disorders Therapeutics Clinical Trials, E7 Countries, 2012* 18
Inherited Metabolic Disorders Therapeutics Market, E7 Countries, Clinical Trials by Trial Status, 2012* 19
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials by Phase, 2012* 20
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials In Progress by Phase 2012* 21
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials by Trial Status, 2012* 22
Inherited Metabolic Disorders Therapeutics Market, Global, Withdrawn Clinical Trials, 2012* 23
Inherited Metabolic Disorders Therapeutics Market, Global, Terminated Clinical Trials, 2012* 24
Inherited Metabolic Disorders Therapeutics Clinical Trials, Global, Average Enrollment Target Trends, 2006-2011 25
Inherited Metabolic Disorders Therapeutics Clinical Trials, Global, Key Sponsors, 2012* 27
Inherited Metabolic Disorders Therapeutics Clinical Trials, Global, Top Companies by Phase, 2012* 29
Inherited Metabolic Disorders Therapeutics Clinical Trials, Global, Clinical Trials by Prominent Drugs, 2012* 30
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Genzyme Corporation, 2012* 31
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Sanofi, 2012* 32
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Synageva BioPharma Corp., 2012* 33
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Shire Plc, 2012* 34
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Raptor Pharmaceuticals Corp., 2012* 35
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Amsterdam Molecular Therapeutics (AMT) Holding N.V., 2012* 36
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Actelion Pharmaceuticals Ltd, 2012* 37
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by U.S. Biotest Inc., 2012* 38
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Edison Pharmaceuticals, Inc., 2012* 39
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Promethera Biosciences S.A., 2012* 40
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by ReceptoPharm, Inc., 2012* 41
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Repligen Corporation, 2012* 42
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Zambon Company S.p.A., 2012* 43
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Actelion Ltd, 2012* 44
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Oregon Health and Science University, 2012* 45
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Masonic Cancer Center, 2012* 46
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Baylor College of Medicine, 2012* 47
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Centre Hospitalier Universitaire de Nice, 2012* 48
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by University of California, San Diego, 2012* 49
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Children's Research Institute, 2012* 50
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by The Children's Hospital Los Angeles, 2012* 51
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by New York Medical College, 2012* 52
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Semmelweis University, 2012* 53
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Peking University, 2012* 54
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Rennes University Hospital, 2012* 55
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by University of Leipzig, 2012* 56
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Children's Hospital Boston, 2012* 57
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by University Hospital Hamburg-Eppendorf, 2012* 58
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Far Eastern Memorial Hospital, 2012* 59
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by University of Sao Paulo, 2012* 60
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Northwestern University, 2012* 61
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by McGill University Health Center, 2012* 62
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by Sheba Medical Center, 2012* 63
Inherited Metabolic Disorders Therapeutics Clinical Trials Market, Global, Clinical Trials by University of Louisville, 2012* 64
List of Figures
List of Figures
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials by Zone (%), 2012* 8
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials by Top Countries, 2012* 9
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials In Progress by Top Countries, 2012* 10
Inherited Metabolic Disorders Therapeutics Clinical Trials, Asia-Pacific, Top Countries (%), 2012* 11
Inherited Metabolic Disorders Therapeutics Clinical Trials, Europe, Top Five Countries (%), 2012* 12
Inherited Metabolic Disorders Therapeutics Clinical Trials, North America, Top Countries (%), 2012* 13
Inherited Metabolic Disorders Therapeutics Clinical Trials, G7 Countries (%), 2012* 16
Inherited Metabolic Disorders Therapeutics Market, G7 Countries, Clinical Trials by Trial Status, 2012* 17
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials by Phase (%), 2012* 20
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials In Progress by Phase, 2012* 21
Inherited Metabolic Disorders Therapeutics Market, Global, Clinical Trials by Trial Status, 2012* 22
Inherited Metabolic Disorders Therapeutics Clinical Trials, Global, Average Enrollment Target Trends, 2006-2011 25
Inherited Metabolic Disorders Therapeutics Clinical Trials, Global, Key Sponsors, 2012* 26
Inherited Metabolic Disorders Therapeutics Clinical Trials, Global, Top Companies by Phase, 2012* 28
Inherited Metabolic Disorders Therapeutics Clinical Trials, Global, Clinical Trials by Prominent Drugs, 2012* 30
GlobalData Methodology 104
Companies Mentioned