- Table of Contents
- List of Tables
- List of Figures
- Global Hemophilia B Pipeline Overview
- Key Findings, 2019
- Disease Overview
- Report Guide and Research Methodology

- Executive Summary
- Hemophilia B Drugs under active development, H1- 2019
- Pipeline Drugs in Early Stage of Development (Pre-clinical, Discovery, Phase 1 and Phase 2)
- Pipeline Drugs in Advanced Stage of Development (Phase 3, Pre-registration)
- Companies involved in Hemophilia B pipeline, H1- 2019
- Mechanism of Action wise Hemophilia B Pipeline Candidates

- Amarna Therapeutics BV Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- ApcinteX Ltd Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Bayer AG Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Bioverativ Inc Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- BloodCenter of Wisconsin Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Catalyst Biosciences Inc Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- China Biologic Products Inc Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- CSL Ltd Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Freeline Therapeutics Ltd Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- GC Pharma Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- LFB SA Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Logicbio Therapeutics Inc Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Novo Nordisk AS Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- OPKO Biologics Ltd Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Pfizer Inc Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Pharming Group NV Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Promethera Biosciences SA Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- RegenxBio Inc Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Sangamo Therapeutics Inc Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Sanofi Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Sigilon Therapeutics Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Spark Therapeutics Inc Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- Takeda Pharmaceutical Co Ltd Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments

- UniQure NV Hemophilia B Pipeline Details
- Business Profile
- Drug Details
• Drug Snapshot
• Originator
• Collaborator/Co-Developer
• Route of Administration
• Orphan Drug/Fast Track/Special Designation
• Area
• Type of Molecular Entity
- Current Status
- Drug Overview
- Drug Mechanism of Action
- Clinical/Pre-clinical Trial Details
- Latest Drug Developments
- Latest Hemophilia B Drug Pipeline Developments, 2019

- Appendix
- About Us
- Sources and Methodology
- Contact Information