Introduction
Batten Disease - Overview
Batten Disease - Therapeutics Development
Batten Disease - Therapeutics Assessment
Batten Disease - Companies Involved in Therapeutics Development
Batten Disease - Drug Profiles
Batten Disease - Dormant Projects
Batten Disease - Discontinued Products
Batten Disease - Product Development Milestones
Appendix

List of Tables
Number of Products under Development for Batten Disease, 2021
Number of Products under Development by Companies, 2021
Number of Products under Development by Universities/Institutes, 2021
Products under Development by Companies, 2021
Products under Development by Universities/Institutes, 2021
Number of Products by Stage and Target, 2021
Number of Products by Stage and Mechanism of Action, 2021
Number of Products by Stage and Route of Administration, 2021
Number of Products by Stage and Molecule Type, 2021
Batten Disease - Pipeline by Abeona Therapeutics Inc, 2021
Batten Disease - Pipeline by Amicus Therapeutics Inc, 2021
Batten Disease - Pipeline by Blue Turtle Bio Technologies Inc, 2021
Batten Disease - Pipeline by Circumvent Pharmaceuticals Inc, 2021
Batten Disease - Pipeline by Collaborations Pharmaceuticals Inc, 2021
Batten Disease - Pipeline by Exicure Inc, 2021
Batten Disease - Pipeline by LEXEO Therapeutics LLC, 2021
Batten Disease - Pipeline by Neurogene Inc, 2021
Batten Disease - Dormant Projects, 2021
Batten Disease - Discontinued Products, 2021

List of Figures
Number of Products under Development for Batten Disease, 2021
Number of Products under Development by Companies, 2021
Number of Products under Development by Universities/Institutes, 2021
Number of Products by Top 10 Targets, 2021
Number of Products by Stage and Top 10 Targets, 2021
Number of Products by Top 10 Mechanism of Actions, 2021
Number of Products by Stage and Top 10 Mechanism of Actions, 2021
Number of Products by Routes of Administration, 2021
Number of Products by Stage and Routes of Administration, 2021
Number of Products by Molecule Types, 2021
Number of Products by Stage and Molecule Types, 2021

Companies Mentioned
• Abeona Therapeutics Inc
• Amicus Therapeutics Inc
• Blue Turtle Bio Technologies Inc
• Circumvent Pharmaceuticals Inc
• Collaborations Pharmaceuticals Inc
• Exicure Inc